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ZAFTUCLENEGENE PIRUPARVOVEC TRANSGENE INSERT

Chemical FDA Substance Registry (openFDA)
Chemical Identification
Known Aliases (1)
Common Name
ZAFTUCLENEGENE PIRUPARVOVEC TRANSGENE INSERT (CODON-OPTIMISED HUMAN PALMITOYL-PROTEIN THIOESTERASE 1 (PPT1, CLN1), UNDER THE CONTROL OF A SYNTHETIC PROMOTER CONSISTING OF A CYTOMEGALOVIRUS (CMV) ENHANCER/CHICKEN .BETA.-ACTIN (CBA) PROMOTER AND A HYBRID INTRON DERIVED FROM CHICKEN .BETA.-ACTIN AND MINUTE VIRUS OF MICE (MVM) INTRONS, FOLLOWED BY A KOZAK SEQUENCE, AND TERMINATED BY A BOVINE GROWTH HORMONE (BGH) POLYADENYLATION (POLYA) SIGNAL)
Data Sources (1)
Source Source ID Name in Source Properties
FDA Substance Registry (openFDA) UA46HCC58W ZAFTUCLENEGENE PIRUPARVOVEC TRANSGENE INSERT FDA UNII: UA46HCC58W
Record Info
IDKJynGFqe3tKFmP8Mv3yN24
CreatedApril 10, 2026, 11:03 p.m.
ModifiedApril 10, 2026, 11:03 p.m.
Data SourceFDA Substance Registry (openFDA)